Gene-fixing treatments have now cured a number of patients with cancer and rare diseases.
In a historic move, the Food and Drug Administration on Tuesday approved a pioneering gene therapy for a rare form of childhood blindness, the first such treatment cleared in the United States for an inherited disease.
Brian Madeux’s life hasn’t been easy. So far, he’s had 26 operations to fix problems in everything from hernias to eyes. He has a rare disease called Hunter syndrome, which is caused by the lack of a gene that’s used to produce an enzyme that breaks down certain carbohydrates. As a result, the carbohydrates build up…
After a disappointing clinical trial in 2015, scientists are trying anew to mend failing hearts with a gene.
Though expensive now, prices could get cheaper for more common diseases.
Lab tests only, so far
The landmark action opens a new chapter in cancer treatment and clears the drug to treat childhood leukemia.
The arrival of gene-therapy cures could transform medicine, but business questions linger.
Motherless babies could be on the horizon after scientists discovered a method of creating offspring without the need for a female egg.
The US Food and Drug Administration’s approval of an engineered herpesvirus for the treatment of melanoma marks the first oncolytic virus to enter the market.
An in-depth look at animal-assisted therapy from a patient’s best friend, Dr. Dog.